An approach to gene therapy is the use of viral vectors to deliver therapeutic genes into a patient's cells. In this method, engineered viruses are modified to carry healthy copies of a gene that is defective or missing in the patient's genome. Once the viral vector enters the target cells, it releases the therapeutic gene, which can then be expressed to produce the correct protein, potentially alleviating symptoms of genetic disorders. Other approaches to gene therapy include CRISPR-Cas9 gene editing, which allows for precise modifications of the genome, and RNA interference (RNAi), which can inhibit the expression of disease-causing genes.
These approaches aim to treat or even cure genetic diseases by correcting the underlying genetic defects.
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